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Terry B. Gernsheimer, Siobhan P Brown, Darrell J Triulzi, et al.
Min Xia, Liron David, Matthew Teater, et al.
4 Safety and Efficacy of CTX001 in Patients with Transfusion-Dependent β-Thalassemia and Sickle Cell Disease: Early Results from the Climb THAL-111 and Climb SCD-121 Studies of Autologous CRISPR-CAS9–Modified CD34+ Hematopoietic Stem and Progenitor Cells
Haydar Frangoul, Yael Bobruff, Maria Domenica Cappellini, et al.
Data from these ongoing studies were submitted on behalf of the CLIMB THAL-111 and CLIMB SCD-121 Investigators.
Kerstin B Kaufmann, Andy G.X. Zeng, Etienne Coyaud, et al
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